Gene Therapy Targets AIDS

Gene Therapy Targets AIDS

Gene Therapy Targets AIDS For many years, a diagnosis of acquired immunodeficiency syndrome (AIDS) was a death sentence. It seemed unthinkable in the 1980s, but the medical community now largely treats the disease as a chronic illness. This profound shift arose...
CRISPR to the People

CRISPR to the People

CRISPR: SNIPPING AWAY AT DISEASE   CRISPR genome editing is one of the most exciting developments in biotechnology since its discovery a few years ago. Bacteria use this mechanism to destroy the DNA of invading viruses. Scientists subsequently discovered CRISPR’s...
New Gene Therapy Drug Explained

New Gene Therapy Drug Explained

New Gene Therapy Drug Explained Novartis’ (Basel, Switzerland) Zolgensma grabbed headlines last week as it garnered the second FDA approval of a gene therapy treatment for an inherited disease. Designed to treat spinal muscular atrophy (SMA), Zolgensa is also set to...
CRISPR Babies

CRISPR Babies

CRISPR Babies Earlier this week, a research team at the Southern University of Science and Technology in Shenzhen, China, announced the birth of twin girls whose genomes had been edited using CRISPR/Cas9. The work was done at an in vitro fertilization clinic prior to...
Gene Therapy Cures

Gene Therapy Cures

The Promise of Gene Therapy Unfolds In many ways, 2017 was the year of gene therapy in the United States. Patients and pharmaceutical companies celebrated the approval of not one, but three treatments for otherwise untreatable health conditions. Researchers have been...
A Drop Of Gene Therapy

A Drop Of Gene Therapy

A Walk In The Park For Hemophilia? Imagine tripping over your feet during a leisurely stroll down the sidewalk. Ouch! Your knees are scraped below your shorts and blood starts to drip. A quick wipe from a conveniently pocketed napkin and soon enough, you are the proud...